Gene and cell therapy of human genetic diseases: Recent advances and future directions

-



alagille syndrome chromosome :: Article Creator


Comments

Post a Comment

Popular posts from this blog

Diagnosis and management of vascular Ehlers-Danlos syndrome: Experience of the UK national diagnostic service, Sheffield | European Journal of Human Genetics

-
Image
blood disease myeloma :: Article Creator Rare Blood Disease Innovations Address Unmet Needs, According To ASH Data Innovations in rare blood disorders took center stage at the 2024 American Society of Hematology (ASH) Annual Meeting & Exposition, with key research presented on immune thrombocytopenia, hemophilia, and multiple myeloma. Innovations in rare blood disorders took center stage at ASH 2024. Image Credit: shidlovski-stock.Adobe.Com Innovations in rare blood disorders took center stage at the 2024 American Society of Hematology (ASH) Annual Meeting & Exposition, with Sanofi highlighting 49 abstracts, including 9 oral presentations, featured at the conference in San Diego.1 Key research was presented on immune thrombocytopenia (ITP), hemophilia, and multiple myeloma (MM), among other disease states. With new findings related to approved and investigational therapies alike, the diverse portfolio demonstrates the e...
Read more

Well-liked Medicare plan vs. higher-ranked providers - ChicagoNow

-
Image
Medicare Open Enrollment ends December 7. The easy choice is to stay with all-in-one Medicare Advantage instead of switching to Traditional Medicare plus a supplement and drug plan. The hard one is whether to switch between Medicare Advantage plans, from a well-liked one to one accepted at a so-called top-10 hospital. Humana Gold Plus, a Medicare Advantage HMO, has served me well for five years. Hearing aids cost me only $10 after its $2,000 allowance. Routine doctor and dentist appointments and my medication cost nothing. But Humana Gold Plus is not accepted by Northwestern Memorial Hospital, the nearby hospital that US News & World Report ranks as the tenth best in the country, or by Northwestern Medicine physicians. My primary care physician is in an Advocate Medical Group. If I were hospitalized, it would be at Advocate Illinois Masonic Medical Center. If I had a serious illness, I’d see specialists in Advocate’s network. Illinois Masonic is not a second-rate hospital, and...
Read more

Leukemia Overview: Symptoms, Signs, Treatment and Causes

-
Image
haemophilia b factor 9 :: Article Creator Long-term Correction Of Canine Hemophilia B By Gene Transfer Of Blood Coagulation Factor IX Mediated By Adeno-associated Viral Vector Lofqvist, T., Nilsson, I.M., Berntorp, E. & Pettersson, H. Haemophilia prophylaxis in young patients—a long term follow up. J. Int. Med. 241, 395–400 (1997). Article  CAS  Google Scholar  Eyster, M.E. Et al. Central nervous system bleeding in hemophiliacs. Blood 51, 1179–1188 ( 1978). CAS  PubMed  Google Scholar  Bray, G.L. & Lubahn, N.L. Hemophilia presenting with–intracranial hemorrhage. An approach to the infant with intracranial bleeding and coagulopathy. Am. J. Dis. Children 141, 1215– 1217 (1987). Article  CAS  Google Scholar  Lusher, J.M. Prophylaxis in children with hemophilia: Is it the optimal treatment? Thromb. Haemost. 78, 726–729 (1997). Article  CAS  PubMed  Google Scholar  Ragni, M.V., Hord, J.D. & Blatt, J. Central ve...
Read more